The BioTech Strategist

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Schlagwort: neurology

  • Merck KGaA-Skyhawk RNA Splicing

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    von

    Aisha Soraya Ahmad
    in

    RNA Splicing Modulation: Analyzing the $2B Merck KGaA-Skyhawk Partnership and the Emergence of a New Therapeutic Modality The human genome contains roughly 20,000 protein-coding genes, yet our bodies produce over 100,000 distinct proteins. This mathematical impossibility becomes reality through RNA splicing, nature’s molecular editing system that rearranges genetic information like a film editor creating different…

  • Kriya Therapeutics $313M Funding

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    von

    Aisha Soraya Ahmad
    in

    Kriya Therapeutics‘ $313M Series Funding: Decoding the Investment Thesis Behind Nine-Asset Gene Therapy Pipelines in a Challenging Market The gene therapy sector exists in a peculiar state of simultaneous crisis and opportunity. On one hand, safety concerns mount as Sarepta’s Elevidys faces scrutiny following patient deaths and the FDA restricts bluebird bio’s Skysona due to…